Vision and Mission
Developing Novel Oligonucleotide Based Therapies
Our primary goal is to develop new therapies that make a meaningful difference in the lives of patients and their families. Our drug development activities focus on:
- UNMET MEDICAL NEEDS including underserved patient populations with neglected, rare, infectious and other diseases.
- SCIENTIFIC INNOVATION based on our pioneering work with novel chemistries for nucleic acid targeted therapeutics.
Beyond developing new medicines, we are committed to making meaningful contributions that improve our community.
- We support programs that provide education and resources to disease communities, including patients, caregivers, and healthcare providers, as well as non-profit organizations focused on the areas in which we do our research.
- We strive to reduce our impact on the environment by applying green business practices in our day-to-day operations.