Vision and Mission

Our Vision

Developing Novel Oligonucleotide Based Therapies

Our primary goal is to develop new therapies that make a meaningful difference in the lives of patients and their families. Our drug development activities focus on:

  • UNMET MEDICAL NEEDS including underserved patient populations with neglected, rare, infectious and other diseases.
  • SCIENTIFIC INNOVATION based on our pioneering work with novel chemistries for nucleic acid targeted therapeutics.

Our Mission

Supporting Communities

Beyond developing new medicines, we are committed to making meaningful contributions that improve our community.

  • We support programs that provide education and resources to disease communities, including patients, caregivers, and healthcare providers, as well as non-profit organizations focused on the areas in which we do our research.
  • We strive to reduce our impact on the environment by applying green business practices in our day-to-day operations.